Caring for Matthew: Managing a Very Rare Disease


Matthew and Family
Read Next

Related News

Luigi's Journey Toward a Better Tomorrow

March 31, 2025 – Luigi's parents faced fear and uncertainty when their son was diagnosed with Lennox-Gastaut syndrome and severe seizures at six months old. Thanks to the compassionate care and innovative treatments at Nicklaus Children’s Hospital, Luigi has made remarkable progress, and his family has opened a PPEC facility to support other families navigating similar challenges.

Lily Shines a Light on the Importance of Early Detection of Neuromotor Delays

March 12, 2025 – Lily, age 2 ½, is walking independently and making remarkable progress, thanks to rehabilitative intervention at Nicklaus Children’s Hospital and an early diagnosis of cerebral palsy.

Leading Pediatric Epilepsy Care for 40 Years

February 26, 2025 – For 40 years, Nicklaus Children's Hospital has been a leader in pediatric epilepsy. Learn more about the comprehensive care we offer for the most complex chronic cases.

Gene Therapy Offers New Hope for Children with Duchenne MD

January 23, 2025 – At Nicklaus Children's Hospital, gene therapy offers a promising treatment that dramatically improves life for children with Duchenne muscular dystrophy. Recognizing the potential wielded by a new gene therapy, Nicklaus Children’s became one of the first in the nation to offer ELEVIDYS-dystrophin soon after the FDA's 2023 approval.